Liver-targeting gene editing achieves significant neurological benefits in MPS I mice


Ou L., Przybilla M., Ahlat O., Overn P., OSullivan G., Kim S., ...More

16th Annual WORLDSymposium, Orlando, Florida, United States Of America, 10 - 13 February 2020, vol.129, pp.124-125, (Summary Text)

  • Publication Type: Conference Paper / Summary Text
  • Volume: 129
  • Doi Number: 10.1016/j.ymgme.2019.11.325
  • City: Orlando, Florida
  • Country: United States Of America
  • Page Numbers: pp.124-125
  • Ankara University Affiliated: Yes