Liver-targeting gene editing achieves significant neurological benefits in MPS I mice
16th Annual WORLDSymposium, Orlando, Florida, United States Of America, 10 - 13 February 2020, vol.129, pp.124-125, (Summary Text)
- Publication Type: Conference Paper / Summary Text
- Volume: 129
- Doi Number: 10.1016/j.ymgme.2019.11.325
- City: Orlando, Florida
- Country: United States Of America
- Page Numbers: pp.124-125
- Ankara University Affiliated: Yes